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Intravenous and Intrathecal Onasemnogene Abeparvovec Gene Therapy in Symptomatic and Presymptomatic Spinal Muscular Atrophy: Long-Term Follow-Up Study

Author:Darras, Basil   Mercuri, Eugenio   Strauss, Kevin   Day, John   Chien, Yin-Hsiu   Masson, Ricardo   Wigderson, Melissa   Alecu, Iulian   Ballarini, Nicolas   Mehl, Lesa   Marra, Jonathan   Connolly, Anne   

Session Name:S34: Child Neurology and Developmental Neurology 2  

Topic:Child Neurology and Developmental Neurology  

Program Number:S34.002  

Author Institution:Boston Children’s Hospital, Harvard Medical School, Boston, MA  Department of Paediatric Neurology and Nemo Clinical Centre, Catholic University, Rome, Italy  Clinic for Special Children, Strasburg, PA  Stanford University School of Medicine, Palo Alto, CA  National Taiwan University Hospital, Taipei City, Taiwan  Fondazione IRCCS Istituto Neurologico Carlo Besta, Milano, Italy  Novartis Gene Therapies, Inc., Bannockburn, IL  Novartis Pharmaceuticals, Basel, Switzerland  Novartis Institutes for BioMedical Research, Cambridge, MA  Novartis Pharmaceuticals, East Hanover, NJ  Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH  

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Stepwise functional brain architecture from disease epicenter correlates with atrophy in progressive supranuclear palsy

Author:Spinelli, Edoardo   Ghirelli, Alma   Bottale, Ilaria   Basaia, Silvia   Cividini, Camilla   Volonte, M. Antonietta   Galantucci, Sebastiano   Magnani, Giuseppe   Caso, Francesca   Canu, Elisa   Castelnovo, Veronica   Caroppo, Paola   Prioni, Sara   Villa, Cristina   Josephs, Keith   Whitwell, Jennifer   Agosta, Federica   Filippi, Massimo   

Session Name:P11: Aging and Dementia: Neuroimaging 1  

Topic:Aging and Dementia  

Program Number:P11.001  

Author Institution:IRCCS San Raffaele Scientific Institute, Milan, Italy  IRCCS San Raffaele Scientific Institute and Vita-Salute San Raffaele University, Milan, Italy  Vita - Salute San Raffaele University, Milan, Italy  Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy  Fondazione IRCCS Istituto Neurologico Carlo Besta, Milano, Italy  Mayo Clinic, Rochester, MN  

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Characterization of FTLD spectrum through advanced diffusion-weighted MRI metrics: a connectome approach

Author:Agosta, Federica   Basaia, Silvia   Facente, Federica   Cividini, Camilla   Spinelli, Edoardo   Canu, Elisa   Castelnovo, Veronica   Magnani, Giuseppe   Caso, Francesca   Caroppo, Paola   Prioni, Sara   Villa, Cristina   Tremolizzo, Lucio   Appollonio, Ildebrando   Silani, Vincenzo   Filippi, Massimo   

Session Name:P11: Aging and Dementia: Neuroimaging 1  

Topic:Aging and Dementia  

Program Number:P11.003  

Author Institution:IRCCS San Raffaele Scientific Institute, Milan, Italy  Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy  Fondazione IRCCS Istituto Neurologico Carlo Besta, Milano, Italy  “San Gerardo” Hospital and University of Milano-Bicocca, Monza, Italy  University of Milan Medical School - IRCCS Istituto Auxologico Italiano, Milan, Italy  Ospedale San Raffaele, Neuroimaging Research Unit, Milan, Italy  

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