Browse All

Current Filters

CLEAR FILTER x

TITLE

Weight Loss and Disease Progression in Amyotrophic Lateral Sclerosis and Primary Lateral Sclerosis

Author:Lee, Ikjae   Mitsumoto, Hiroshi   Factor-Litvak, Pam   Nieves, Jeri   

Session Name:P2: Neuromuscular Disease: ALS, SMA, and Other Motor Neuron Disorders 1  

Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

Program Number:P2.009  

Author Institution:Columbia University Irving Medical Center, New York, NY  Mailman School of Public Health, New York, NY  

Treatment Effects Among Patients with Type 2 and Type 3 SMA Directly Reported by Patients and Caregivers from the TOPAZ Clinical Trial

Author:Pokrzywinski, Robin   Cutts, Katelyn   Shah, Hemal   Kertesz, Nathalie   Lesh, Sabrina   Sadanowicz, Mara   Song, Guochen   O'Neil, Janet   Barrett, Doreen   Barnobi, Erin   Baver, Scott   

Session Name:P2: Neuromuscular Disease: ALS, SMA, and Other Motor Neuron Disorders 1  

Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

Program Number:P2.010  

Author Institution:Patient-Centered Research, Evidera, Bethesda, MD  alue Matters, LLC. New York, NY  Scholar Rock, Inc. Cambridge, MA  

Assessment of Transition Plan Implementation and Provider Engagement Amongst Adults Affected by Spinal Muscular Atrophy (SMA)

Author:Eisenman, Lauren   Curry, Mary   Belter, Lisa   Jarecki, Jill   Schroth, Mary   

Session Name:P2: Neuromuscular Disease: ALS, SMA, and Other Motor Neuron Disorders 1  

Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

Program Number:P2.011  

Author Institution:Cure SMA, Elk Grove Village, IL  Cure SMA, San Diego, CA  

Comparing Spinal Muscular Atrophy (SMA) outcomes between a patient-reported membership database and a clinical data registry

Author:Belter, Lisa   Whitmire, Sarah   Curry, Mary   Schroth, Mary   

Session Name:P2: Neuromuscular Disease: ALS, SMA, and Other Motor Neuron Disorders 1  

Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

Program Number:P2.012  

Author Institution:Cure SMA, Elk Grove Village, IL  

The Use of Onasemnogene-abeparvovec at 33 weeks’ gestation in Spinal Muscular Atrophy with One Copy of SMN2

Author:Ajjarapu, Aparna   Mathews, Katherine   Ramachandra, Divya   

Session Name:P2: Neuromuscular Disease: ALS, SMA, and Other Motor Neuron Disorders 1  

Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

Program Number:P2.013  

Author Institution:University of Iowa Carver College of Medicine , Iowa City , IA  Advocate Children’s Hospital, Oak Lawn , IL