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              PGN-EDO51: Preclinical Data Supporting the Development of an Enhanced Delivery Oligonucleotide (EDO) for the Treatment of Duchenne Muscular Dystrophy (DMD)

              Author:Holland, Ashling   Godfrey, Caroline   Lonkar, Pallavi   Svenstrup, Niels   Larkindale, Jane   McArthur, James   Bracegirdle, Sonia   Goyal, Jaya   

              Session Name:P3: Neuromuscular Disease: Inherited Muscle Disorders 1  

              Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

              Program Number:P3.002  

              Author Institution:PepGen Inc., Cambridge, MA  

              PGN-EDO51, an Enhanced Delivery Oligonucleotide (EDO) for the Treatment of Duchenne Muscular Dystrophy (DMD): Results of a Phase 1 Study in Healthy Volunteers

              Author:Mellion, Michelle   Larkindale, Jane   Lonkar, Pallavi   Goyal, Jaya   Holland, Ashling   Foy, Jeff   Garg, Brijesh   Yu, Shaoxia   Frank, Anthony   Abbott, Chris   Svenstrup, Niels   Cormier, Jennifer   Vacca, Sarah   McArthur, James   

              Session Name:P3: Neuromuscular Disease: Inherited Muscle Disorders 1  

              Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

              Program Number:P3.004  

              Author Institution:PepGen Inc., Cambridge, MA  

              Design of a Phase 1, Placebo-Controlled Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Single-Ascending Doses of PGN-EDODM1 in Adult Participants with Myotonic Dystrophy Type 1 (DM1)

              Author:Mellion, Michelle   Larkindale, Jane   Cormier, Jennifer   Hand, Holly   Vacca, Sarah   Lonkar, Pallavi   Holland, Ashling   Garg, Brijesh   Foy, Jeff   McArthur, James   

              Session Name:P6: Neuromuscular Disease: Inherited Muscle Disorders 3  

              Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

              Program Number:P6.004  

              Author Institution:PepGen Inc., Cambridge, MA