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International Delphi Survey of Clinical Practice in Stiff Person Syndrome and Related Disorders: Terminology and Diagnosis

Author:Yoji Hoshina  Ka-Ho Wong  Sadie McGreer  Justin Abbatemarco  Bettina Balint  Kyle Blackburn  Stefan Blum  Adrian Budhram  Marinos Dalakas  Josep Dalmau  Livia Dutra  Francesc Graus  Jerome Honnorat  Takahiro Iizuka  Sarosh Irani  Saiju Jacob  Eric Lancaster  Jenny Linnoila  Alfonso Lopez  Sara Mariotto  Naoko Matsui  Andrew McKeon  Joao Moura  Scott Newsome   O'  Orna Toole  Amanda Piquet  Amy Quek  Albert Saiz  Mateus Simabukuro  Claudia Sommer  Maarten Titulaer  Alberto Vogrig  Yujie Wang  Tara Zier  Jacqueline Kraska  Giovanna Manzano  Anastasia Zekeridou  Stacey Clardy  

Topic:Autoimmune Neurology  

Program Number:C16.002  P2.048  

Author Institution:University of Utah Health, Cambridge, MA  U of U Neurology Clinic, Salt Lake City, UTCleveland Clinic, Beachwood, OH  University Hospital of Zurich, Zurich, Switzerland  University of Texas Southwestern Medical Center, Dallas, TX  Princess Alexandra Hospital, Ipswich Road, Australia  London Health Sciences Centre, London, ON, Canada  Thomas Jefferson University, Philadelphia, PA  IDIBAPS, Barcelona, Spain  Hospital Israelita Albert Einstein, Sao Paulo, Brazil  Hospices Civils de Lyon, Lyon, France  Department of Neurology, Kitasato University School of Medicine, Sagamihara, Japan  Mayo Clinic, Jacksonville, FL  University Hospitals Birmingham NHS Foundation Trust, Birmingham, United Kingdom  The University of Pennsylvania, Dept. of Neurology, Philadelphia, PA  University Neurology Associates, UPMC, Pittsburgh, PA  Neurology Unit, University of Verona, Verona, Italy  Tokushima University, Tokushima, Japan  Mayo Clinic, Rochester, MN  Centro Hospitalar Universitá  rio do Porto, Porto, Portugal  Johns Hopkins Hospital, Baltimore, MD  Mercy University Hospital, Cork, Ireland  University of Colorado, Aurora, CO  National University Hospital, Singapore, Singapore  Hospital Clinico De Barcelona, Barcelona, Spain  Hospital Das Clinicas, Sao Paulo U Scho of Med, Sao Paulo, Brazil  Neurologische Klinik der Universitat, Wü  rzburg, Germany  Erasmus Medical Center, Rotterdam, Netherlands  University of Udine, Udine, Italy  UW Northwest, Seattle, WA  The Stiff Person Syndrome Research Foundation, Bethesda, MDUniversity of California Irvine, Ladera Ranch, CA  Neuroimmunology Laboratory, Mayo Clinic, Rochester, MN  University of Utah, Salt Lake City, UT  

International Delphi Survey of Clinical Practice in Stiff Person Syndrome and Related Disorders: Treatment and Monitoring

Author:Yoji Hoshina  Ka-Ho Wong  Sadie McGreer  Justin Abbatemarco  Bettina Balint  Kyle Blackburn  Stefan Blum  Adrian Budhram  Marinos Dalakas  Josep Dalmau  Livia Dutra  Francesc Graus  Jerome Honnorat  Takahiro Iizuka  Sarosh Irani  Saiju Jacob  Eric Lancaster  Jenny Linnoila  Alfonso Lopez  Sara Mariotto  Naoko Matsui  Andrew McKeon  Joao Moura  Scott Newsome   O'  Orna Toole  Amanda Piquet  Amy Quek  Albert Saiz  Mateus Simabukuro  Claudia Sommer  Maarten Titulaer  Alberto Vogrig  Yujie Wang  Tara Zier  Jacqueline Kraska  Giovanna Manzano  Anastasia Zekeridou  Stacey Clardy  

Topic:Autoimmune Neurology  

Program Number:P2.047  

Author Institution:University of Utah Health, Cambridge, MA  U of U Neurology Clinic, Salt Lake City, UTCleveland Clinic, Beachwood, OH  University Hospital of Zurich, Zurich, Switzerland  University of Texas Southwestern Medical Center, Dallas, TX  Princess Alexandra Hospital, Ipswich Road, Australia  London Health Sciences Centre, London, ON, Canada  Thomas Jefferson University, Philadelphia, PA  IDIBAPS, Barcelona, Spain  Hospital Israelita Albert Einstein, Sao Paulo, Brazil  Hospices Civils de Lyon, Lyon, France  Department of Neurology, Kitasato University School of Medicine, Sagamihara, Japan  Mayo Clinic, Jacksonville, FL  University Hospitals Birmingham NHS Foundation Trust, Birmingham, United Kingdom  The University of Pennsylvania, Dept. of Neurology, Philadelphia, PA  University Neurology Associates, UPMC, Pittsburgh, PA  Neurology Unit, University of Verona, Verona, Italy  Tokushima University , Tokushima, Japan  Mayo Clinic, Rochester, MN  Centro Hospitalar Universitá  rio do Porto, Porto, Portugal  Johns Hopkins Hospital, Baltimore, MD  Mercy University Hospital, Cork, Ireland  University of Colorado, Aurora, CO  National University Hospital, Singapore, Singapore  Hospital Clinico De Barcelona, Barcelona, Spain  Hospital Das Clinicas, Sao Paulo U Scho of Med, Sao Paulo, Brazil  Neurologische Klinik der Universitat, Wü  rzburg, Germany  Erasmus Medical Center, Rotterdam, Netherlands  University of Udine, Udine, Italy  UW Northwest, Seattle, WA  The Stiff Person Syndrome Research Foundation, Bethesda, MDUniversity of California Irvine, Ladera Ranch, CA  Neuroimmunology Laboratory, Mayo Clinic, Rochester, MN  University of Utah, Salt Lake City, UT  

Update on Phase 2 of KYSA-6, an Open-label, Single-arm, Multicenter Phase 2/3 Study of Miv-cel (Mivocabtagene Autoleucel; KYV-101), a Fully Human CD19 Chimeric Antigen Receptor (CAR) T-cell Therapy in Generalized Myasthenia Gravis (gMG)

Author:Marinos Dalakas  Srikanth Muppidi  Michael Hunter  Sarah Hoffmann  Tobias Hegelmaier  Jeremias Motte  Ralf Gold  Charlotte Schubert  Bradley Hunter     tter-Krö  Marie Luise nke  Christian Schultze-Florey  Roland Schroers  Francis Ayuk  Justin Chou  Xue Han  John Sun  Shouvonik Sengupta  Christine Bryant  Linus Sun  Dena Grayson  Naji Gehchan  Aiden Haghikia  

Topic:Autoimmune Neurology  

Program Number:P3.012  

Author Institution:Department of Neurology, Thomas Jefferson University, Philadelphia, PA  Department of Neurology, Stanford Healthcare, Stanford, CA  Department of Neuromuscular Medicine, Intermountain Medical Center, Murray, UT  Department of Neurology with Experimental Neurology and Neuroscience Clinical Research Center (NCRC), Charité  -Universitä  tsmedizin Berlin, 10117 Berlin, Germany  Department of Neurology with Clinical Neurophysiology, Hannover Medical School, Hannover, Germany  Department of Neurology, Ruhr University Bochum, Bochum, Germany  Institute of Neuroimmunology and Multiple Sclerosis and Department of Neurology, University Medical Center Hamburg-Eppendorf, Hamburg, Germany  Department of Hematology Oncology, Blood and Marrow Transplantation, Intermountain LDS Hospital, Salt Lake City, UT  Department of Hematology, Oncology and Cancer Immunology, Charité  Universitä  tsmedizin Berlin, Berlin, Germany  Department of Hematology, Hemostaseology, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany  Department of Hematology and Oncology, Ruhr University Bochum, Bochum, Germany  Department for Stem Cell Transplantation, University Medical Center Hamburg-Eppendorf, Hamburg, Germany  Kyverna Therapeutics, Inc., Emeryville, CA