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Safety and Efficacy of DYNE-251 in Males with DMD Mutations Amenable to Exon 51 Skipping

Author:Shieh, Perry   Campbell, Craig   Deconink, Nicolas   De Waele, Liesbeth   Flanigan, Kevin   Lorentzos, Michelle   Phan, Han   Mix, Chris   Ray, Soma   Wang, Dazhe   Dugar, Ashish   Kerr, Douglas   Naylor, Maria   Guglieri, Michela   

Session Name:S31: Hot Topics in Child Neurology  

Topic:Child Neurology and Developmental Neurology  

Program Number:S31.010  

Author Institution:University of California Los Angeles, Los Angeles, CA  London Health Sciences Centre, London, ON, Canada  Neuromuscular Reference Center UZ Gent, Gent, Belgium  University Hospitals Leuven, Leuven, Belgium  Nationwide CHildrens Hospital, Columbus, OH  Children's Hospital at Westmead, Westmead, New South Wales, Australia  Rare Disease Research, LLC, Atlanta, GA  Dyne Therapeutics, Inc., Waltham, MA  Royal Victoria Infirmary, Newcastle University, Newcastle-Upon-Tyne, United Kingdom  

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Symmetry of Sleep Spindles Predicts Surgical Outcomes in Corpus Callosotomy

Author:Abata, Joshua   Jiang, Mio   Ho, Victoria   Vadera, Sumeet   Sazgar, Mona   Mnatsakanyan, Lilit   Jung, Brian   

Session Name:P3: Epilepsy/Clinical Neurophysiology (EEG): EEG and Neurophysiology  

Topic:Epilepsy/Clinical Neurophysiology (EEG)  

Program Number:P3.010  

Author Institution:University of California, Irvine, Orange, CA  University of California Los Angeles, Los Angeles, CA  

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Understanding the Impact of Parkinson’s Disease in Zambia: An Assessment of Patient and Caregiver Needs

Author:Adrissi, Jennifer   Jules, Rebecca   Shen, Vivian   Vinegar, Jessica   Chishimba, Lorraine   Saylor, Deanna   

Session Name:P6: Global Neurology  

Topic:Global Health and Neuroepidemiology  

Program Number:P6.010  

Author Institution:University of California Los Angeles, Los Angeles, CA  University Teaching Hospital, Zambia, Lusaka, Zambia  Johns Hopkins Hospital, Baltimore, MD  

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Clarification of the Mechanism of Action of Cenobamate

Author:Sankar, Raman   Ferrari, Louis   

Session Name:P9: Epilepsy/Clinical Neurophysiology (EEG): Anti-seizure Medications: Mechanisms and Pharmacology  

Topic:Epilepsy/Clinical Neurophysiology (EEG)  

Program Number:P9.012  

Author Institution:University of California Los Angeles, Los Angeles, CA  SK Life Science, Inc., Paramus, NJ  

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