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The Path to Diagnosis and Treatment Among Patients With Generalized Myasthenia Gravis (gMG): Health Disparities Experienced by Racial and Ethnic Minorities From Project ASPIRE (eliminAte diSparities and Promote equIty in Rare diseasE)

Timing and Frequency of Onset Symptoms in Friedreich Ataxia Based on Real-world Medical Claims Data

Progression of Friedreich Ataxia to Scoliosis and Cardiomyopathy: Utility of Real-World Data From Medical Claims