Lifesaving Treatments for Spinal Muscular Atrophy: Global Access and Availability

Author:Armengol, Victor   Darras, Basil   Abulaban, Ahmad   Alshehri, Ali Mohammed   Barisic, Nina   Ben-Omran, Tawfeg   Bernert, Gunther   Castiglioni, Claudia   Chien, Yin-Hsiu   Farrar, Michelle   Kandawasvika, Gwendoline Quetoline   Khadilkar, Satish   Mah, Jean   Marini-Bettolo, Chiara   Osredkar, Damjan   Pfeffer, Gerald   Piazzon, Flavia   Pitarch Castellano, Inmaculada   Quijano-Roy, Susana   Saito, Kayoko   Shin, Jin-Hong   Vázquez-Costa, Juan   Walter, Maggie   Wanigasinghe, Jithangi   Xiong, Hui   Griggs, Robert   Roy, Bhaskar   

Session Name:P5: Health Care Disparities: Movement, Neuromuscular, MS, and Headache  

Topic:Health Care Disparities  

Program Number:P5.003  

Author Institution:Yale School of Medicine, New Haven, CT  Children'S Hosp Boston Harvard Med School, Boston, MA  King Saud Bin Abdulaziz University for Health Sciences, Riyadh, Saudi Arabia  King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia  University Hospital Centre Zagreb, Zagreb, Croatia  Sidra Medicine and Hamad Medical Corporation, Doha, Qatar  Klinik Favoriten, Vienna, Austria  Clínica Meds, Santiago, Chile  National Taiwan University Hospital, Taipei, Taiwan  University of New South Wales, Sydney, Australia  University of Zimbabwe, Harare, Zimbabwe  Bombay Hospital, Mumbai, India  University of Calgary, Calgary, AB, Canada  Newcastle University, Newcastle Upon Tyne, United Kingdom  University Medical Centre, Ljubljana, Slovenia  University of Sao Paulo, Sao Paulo, Brazil  Hospital Universitari i Politècnic La Fe, Valencia, Spain  APHP Université Paris Saclay, Hôpital Raymond Poincaré, Garches, France  Tokyo Women’s Medical University, Tokyo, Japan  Pusan National University Yangsan Hospital, Yangsan, Korea, Republic of  Hospital Universitario y Politécnico La Fe, Valencia, Spain  Ludwig-Maximilians-University of Munich, Munich, Germany  University of Colombo, Colombo, Sri Lanka  Peking University First Hospital, Beijing, China, People's Republic of  University of Rochester Medical Center, Rochester, NY