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47-year-old with Brain and Spinal Cord Lesion: an Atypical Presentation of CADASIL

90-month Muscle Function and Biomarker Outcomes With Cipaglucosidase Alfa Plus Miglustat (Cipa+Mig) in Adults With Pompe Disease in ATB200-02, an Open-label Phase I/II Study

Access to High-efficacy Therapies for Multiple Sclerosis Under Medicaid: Variation in Coverage and Utilization Across States

Author:Kakara, Mihir   

Session Name:S12: Practice, Policy, and Ethics  

Topic:Child Neurology and Developmental Neurology  

Program Number:S12.001  

Author Institution: