Beyond Motor Function in Adults With Spinal Muscular Atrophy (SMA): A Systematic Literature Review of Real-world Outcomes With Risdiplam

Real-world Motor Function Outcomes with Risdiplam in Types 2 and 3 Spinal Muscular Atrophy (SMA): A Systematic Literature Review and Meta-analysis

Exploration of the Diagnostic and Treatment Journey of Adult-onset (Type Four) SMA

Exploration of Patient and Caregiver Burden Due to Insurance Denials and Appeals for Spinal Muscular Atrophy (SMA) Treatment and Healthcare Access

Long-term Efficacy and Safety of Risdiplam in Adults With 5q Spinal Muscular Atrophy (SMA): A Large Prospective Multi-centre Observational Study