Design and Rationale of TRITON-PN, a Phase Three Study to Evaluate the Efficacy of Nucresiran in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy

Author:Obici, Laura Piera   Cárdenas-Soto, Karla   Waddington-Cruz, Marcia   Plante-Bordeneuve, Violaine   Losada, Ines   Brannagan, Thomas   Gillmore, Julian   Berk, John   Li, JuanJuan   Lau, K. H. Vincent   Gonzalez-Duarte, Alejandra   

Session Name:P6: Neuromuscular and Clinical Neurophysiology (EMG): Peripheral Nerve and Other Neuromuscular Disorders  

Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

Program Number:Neuromuscular and Clinical Neurophysiology (EMG)  

Author Institution:Amyloidosis Research and Treatment Centre, IRCCS Fondazione Policlinico San Matteo, Pavia, Italy, Pavia, Italy  Instituto Nacional de Ciencias Médicas y Nutrición Salvador Zubirán, Tlalpan, Mexico, Tlalpan, Mexico  Hospital Universitário Clementino Fraga Filho, Centro de Estudos em Paramiloidose Antônio Rodrigues de Mello, Universidade Federal do Rio de Janeiro, Rio de Janeiro, Brazil, Brazil  Neurology - Amyloid Network, CHU Henri Mondor, APHP, University Paris Est - Créteil, Créteil, France, Creteil, France  Hospital Universitario Son Llatzer, Instituto de Investigación Sanitaria Illes Balears, Palma de Mallorca, Spain, Spain  Columbia University, New York, NY, USA, New York, NY  National Amyloidosis Centre, University College London, Royal Free Hospital, London, UK, United Kingdom  Boston University School of Medicine, Boston, MA, USA, MA  Alnylam Pharmaceuticals, Cambridge, MA, USA, MA  NYU School of Medicine, New York, NY, USA, NY  

Diagnostic Patterns and Clinical Characteristics of Hereditary ATTR Amyloidosis: A Retrospective Study From a U.S. Health System