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Phase I Study of RAG-17, an siRNA Therapy Targeting SOD1, in Patients with SOD1-ALS: Preliminary Safety, Biomarker and Efficacy Data

Author:Wu, Zhi-Ying   Li, Hong-Fu   Chen, Wei-Qi   Shang, Hui-Fang   Wei, Qian-Qian   Zhang, Xiaoxue   Chen, Qiwen   Zhang, Caiqin   Kang, Moorim   Li, Long-Cheng   Wang, Yi-Long   

Session Name:P2: Emerging Science 1  

Topic:General Neurology  

Program Number:P2.018  

Author Institution:Second Affiliated Hospital, Zhejiang University School of Medicine, Hangzhou, China, People's Republic of  Capital Medical University, China, People's Republic of  West China Hospital of Sichuan University, China, People's Republic of  Ractigen Therapeutics, China, People's Republic of  

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Adherence and Safety of Intravenous Inebilizumab for NMOSD: Real-world Evidence from China

Author:Zhang, Ying   Wang, Rui   Chen, Hongxi   Shi, Ziyan   Du, Qin   Zhou, Hongyu   

Session Name:P6: Autoimmune Neurology: NMOSD/MOGAD 5  

Topic:Autoimmune Neurology  

Program Number:P6.006  

Author Institution:West China Hospital of Sichuan University, Chengdu, China, People's Republic of  West China Hospital of Sichuan University, China, People's Republic of  

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