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  • PDMA Neuroscience and Rare Disease, F. Hoffmann-La Roche Ltd, Basel, Switzerland, Switzerland

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Beyond Motor Function in Adults With Spinal Muscular Atrophy (SMA): A Systematic Literature Review of Real-world Outcomes With Risdiplam

Author:Guittari, Carol Jean   Gorni, Ksenija   Sideris, Eleftherios   Davies, Evan   Mahajan, Anadi   Kumari, Sandhya   Simpson, Alex   Sutherland, C. Simone   

Session Name:P5: Neuromuscular and Clinical Neurophysiology (EMG): Motor Neuron Disorders  

Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

Program Number:P5.001  

Author Institution:PDMA Neuroscience and Rare Disease, Genentech, Inc., South San Francisco, CA, USA, South San Francisco, CA  PDMA Neuroscience and Rare Disease, F. Hoffmann-La Roche Ltd, Basel, Switzerland, Switzerland  Global Access, F. Hoffmann-La Roche Ltd, Basel, Switzerland, Switzerland  Bridge Medical Consulting Ltd., London, UK, United Kingdom  

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Real-world Motor Function Outcomes with Risdiplam in Types 2 and 3 Spinal Muscular Atrophy (SMA): A Systematic Literature Review and Meta-analysis

Author:Guittari, Carol Jean   Davies, Evan   Sutherland, C. Simone   Gorni, Ksenija   Edwards, Susan   Kjærgaard, Maya   Mahajan, Anadi   Gupta, Digant   Khan, Mudasir   Kumari, Sandyha   Sideris, Eleftherios   

Session Name:P5: Neuromuscular and Clinical Neurophysiology (EMG): Motor Neuron Disorders  

Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

Program Number:P5.002  

Author Institution:Genentech Inc, CA, USA, South San Francisco, CA  Global Access, F. Hoffmann-La Roche Ltd, Basel, Switzerland, Switzerland  PDMA Neuroscience and Rare Disease, F. Hoffmann-La Roche Ltd, Basel, Switzerland, Switzerland  Pharma Development, Data Sciences, F. Hoffmann-La Roche Ltd, Basel, Switzerland, Switzerland  Roche Pharmaceuticals AS, Copenhagen, Denmark, Denmark  Bridge Medical Consulting Ltd, London, UK, United Kingdom  

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