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Phase II/III Study of Ulviprubart in Inclusion Body Myositis: Study Design, Patient Characteristics, and Topline Results

Author:Goyal, Namita A.   Machado, Pedro M.   Ascherman, Dana P.   Benveniste, Olivier   Beydoun, Said R.   Brannagan, Thomas H.   Christopher-Stine, Lisa   Collins, Michael P.   De Bleecker, Jan L.   Dimachkie, Mazen   Dixon, Stacy   Fernandez, David R.   Freimer, Miriam   Geiger, Christopher   Gonzalez-Perez, Paloma   Goyal, Neelam   Gwathmey, Kelly   Heitzman, Daragh   Henderson, Robert D.   Hodson-Webb, Lisa D.   Hussain, Yessar   Korngut, Lawrence   Liang, Christina   Lilleker, James B.   Lloyd, Thomas   Mohassel, Payam   Naddaf, Elie   Needham, Merrilee   Piccione, Ezequiel   Quinn, Colin C.   Rosow, Laura   Roy, Bhaskar   Ruck, Tobias   Schmidt, Jens   Seth, Arjun   Shah, Jaimin   Shaibani, Aziz   Shieh, Perry B.   Simmons, Zachary   Sivakumar, Kumaraswamy   Wang, Leo H.   Weihl, Conrad C.   Wilkins, H. Jeffrey   Amato, Anthony   

Session Name:S7: Updates on Muscle Disorders  

Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

Program Number:S7.007  

Author Institution:Department of Neurology, University of California Irvine, Orange, CA, USA, Orange, CA  Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology, University College London, London, UK  NIHR University College London Hospitals Biomedical Research Centre, University College London Hospitals NHS Foundation Trust, London, UK, London, United Kingdom  Department of Medicine, University of Pittsburgh School of Medicine, Pittsburgh, PA, USA, Pittsburgh, PA  Department of Internal Medicine and Clinical Immunology, Pitié-Salpêtrière University Hospital, Sorbonne Université, AP-HP, Paris, France, Paris, France  University of Southern California, Los Angeles, CA, USA, Los Angeles, CA  Neurological Institute, Columbia University Medical Center, New York, NY, USA, New York, NY  Johns Hopkins University School of Medicine, Baltimore, MD, USA, Baltimore, MD  Medical College of Wisconsin, Milwaukee, WI, USA, Milwaukee, WI  Department of Neurology and Neuromuscular Reference Center, Ghent University Hospital, Ghent, Belgium, Ghent, Belgium  Department of Neurology, The University of Kansas Medical Center, Kansas City, KS, USA, Kansas City, KS  University of Colorado, Aurora, CO, USA, Aurora, CO  Department of Rheumatology, Hospital for Special Surgery, New York, NY, USA, New York, NY  Department of Neurology, The Ohio State Wexner Medical Center, Columbus, OH, USA, Columbus, OH  University Hospitals-Cleveland Medical Center, Case Western Reserve University, Cleveland, OH, USA, Cleveland, OH  Department of Neurology, Massachusetts General Hospital, Harvard Medical School, Boston, MA, USA, Boston, MA  Stanford Neuroscience Health Center, Palo Alto, CA, USA, Palo Alto, CA  Department of Neurology, Virginia Commonwealth University, Richmond, VA, USA, Henrico, VA  Texas Neurology, Dallas, TX, USA, Dallas, TX  Department of Neurology, Royal Brisbane and Women's Hospital, Brisbane, Australia  Centre for Clinical Research, University of Queensland, Brisbane, Australia, Brisbane, Australia  Neuromuscular Division/Department of Neurology, Duke University, Durham, NC, USA, Durham, NC  Austin Neuromuscular Center, Austin, TX, USA, Austin, TX  Hotchkiss Brain Institute, Department of Clinical Neurosciences, Cumming School of Medicine, University of Calgary, Alberta, Canada, Calgary, AB, Canada  Faculty of Medicine and Health, University of Sydney, Camperdown, New South Wales, Australia  Department of Neurology, Royal North Shore Hospital, Northern Sydney Local Health District, Sydney, New South Wales Australia  Neuroscience Research Australia, Sydney, New South Wales, Australia, Australia  Manchester Centre for Clinical Neurosciences, Northern Care Alliance NHS Foundation Trust, Salford, UK  The University of Manchester, Manchester, UK, United Kingdom  Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, MD, USA  Department of Neurology, Baylor College of Medicine, Houston, TX, USA  Department of Clinical Research, Imricor Medical Systems, Burnsville, MN, USA, Houston, TX  Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, MD, USA, Baltimore, MD  Department of Neurology, Mayo Clinic, Rochester, MN, USA, Rochester, MN  Perron Institute, QEII Medical Centre, Nedlands, Western Australia, Australia  University of Notre Dame, Perth, Western Australia, Australia  Fiona Stanley Hospital, Perth, Western Australia, Australia  Murdoch University, Perth, Western Australia, Australia, Murdoch, Australia  Department of Neurology, University of Nebraska Medical Center, Omaha, NE, USA, Omaha, NE  Neuromuscular Division, Neurology Department, University of Pennsylvania, Philadelphia, PA, USA, PA  University of California San Francisco, San Francisco, CA, USA, San Francisco, CA  Department of Neurology, Yale School of Medicine, New Haven, CT, USA, New Haven, CT  Ruhr University Bochum, BG-University Hospital Bergmannsheil Department of Neurology, Bochum, Germany  Heimer Institute for Muscle Research, BG-University Hospital Bergmannsheil Department of Neurology, Bochum, Germany, Düsseldorf, Germany  Department of Neurology, Neuromuscular Center, University Medical Center Göttingen, Göttingen, Germany  Department of Neurology and Pain Treatment, Neuromuscular Center, Center for Translational Medicine, Immanuel University Hospital, Brandenburg Medical School, Rüdersdorf bei Berlin, Germany, Rüdersdorf bei Berlin, Germany  Department of Neurology, Northwestern Memorial Hospital, Chicago, IL, USA, Chicago, IL  Department of Neurology, Mayo Clinic, Jacksonville, FL, USA, Jacksonville, FL  Nerve and Muscle Center of Texas, Houston, TX, USA, Houston, TX  Department of Pediatrics, University of California Los Angeles, Los Angeles, CA, USA, Los Angeles, CA  Department of Neurology, Penn State University College of Medicine, Hershey, PA, USA, Hershey, PA  The Neuromuscular Research Centre and Neuromuscular Clinic of Arizona, Phoenix, AZ, USA, Paradise Valley, AZ  Department of Neurology, University of Washington, Seattle, WA, USA, WA  Department of Neurology, Washington University in St Louis, St Louis, MO, USA, MO  Abcuro, Inc., Newton, MA, USA, MA  Brigham and Women’s Hospital, Harvard Medical School, Boston, MA, USA, Boston, MA  

Clinical and Post-acute Features of Powassan Virus Encephalitis in a High-volume Northeastern Hospital System

Safety and Tolerability of GTX-104 (Nimodipine Injection for IV Infusion) Compared With Oral Nimodipine in Patients With Aneurysmal Subarachnoid Hemorrhage: A Prospective, Randomized Trial