Browse All

Current Filters

CLEAR FILTER x

TITLE

GHF-201, A Novel Oral Compound for Adult Polyglucosan Body Disease, Demonstrates Promising Safety and Efficacy in a Compassionate Use Program

Author:Kakhlon, Or   Mordechai, Anat   Garti, Nissim   Gilgun-Sherki, Yossi   Weil, Miguel   Lossos, Alexander   

Session Name:S2: Updates on Motor Neuron and Peripheral Nerve Disorders  

Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

Program Number:S2.010  

Author Institution:Hadassah Hospital, Jerusalem, Israel  Lyotropic Delivery Systems Ltd, Jerusalem, Israel  Golden Heart Flower, Afula, Israel  Tel-Aviv University, Tel Aviv, Israel  

A Phase 2/3 Adaptive Design Study of GHF-201 as the First Potential Treatment of Adult Polyglucosan Body Disease

Author:Hirano, Michio   Weil, Miguel   Kakhlon, Or   Mordechai, Anat   Garti, Nissim   Gilgun-Sherki, Yossi   Lossos, Alexander   

Session Name:P5: Neuromuscular and Clinical Neurophysiology (EMG): Motor Neuron Disorders  

Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

Program Number:P5.014  

Author Institution:Columbia University Medical Center, New York, NY  Tel-Aviv University, Tel Aviv, Israel  Hadassah Hospital, Jerusalem, Israel  Lyotropic Delivery Systems Ltd, Jerusalem, Israel  Golden Heart Flower, Afula, Israel