Browse All

Current Filters

CLEAR FILTER x

TITLE

Deramiocel Significantly Slows Upper Limb Functional Decline in Duchenne Muscular Dystrophy: Skeletal Muscle Outcomes from the Phase 3 HOPE-3 Trial

Author:Iannaccone, Susan   McDonald, Craig   Veerapandiyan, Aravindhan   Varadhachary, Arun   Ramos-Platt, Leigh   Gambetta, Kathryn   Butterfield, Russell   Leffler, Mindy   maharry, kati   Hogan, Nathaniel J.   apkon, susan   Tian, Cuixia   Mathews, Katherine   Bass, Nancy   Laverty, Chamindra   Phan, Han   Ghosh, Partha   Perlman, Seth   Scharf, Rebecca   mosher, Kathryn   Bernes, Saunder   emerson, Jane   Smith, Edward   Binks, Michael   Awadalla, Mark   Marban, Linda   

Session Name:LS2: Late-breaking Science 2  

Topic:Child Neurology and Developmental Neurology  

Program Number:LS2.003  

Author Institution:Department of Pediatrics, Dallas, TX  UC Davis Dept. of PM&R, Sacramento, CA  Arkansas Childrens Hospital/UAMS, Little Rock, AR  Washington University in St Louis, Saint Louis, MO  USC/Children'S Hospital of Los Angeles, Los Angeles, CA  Ann & Robert H. Lurie Children’s Hospital of Chicago, Chicago, IL  University of Utah, Salt Lake City, UT  Consultant, WA  Capricor Therapeutics Inc, NC  Capricor Therapeutics Inc., UT  Children's Hospital Colorado, CO  Cincinnati Childrens Hospital Medical Center, Cincinnati, OH  University of Iowa - Dept of Pediatrics, Iowa City, IA  Children's Wisconsin, Milwaukee, WI  UC San Diego, San Diego, CA  Rare Disease Research, LLC, Atlanta, GA  Boston Children'S Hospital, Boston, MA  Seattle Children's Hospital, Seattle, WA  University of Virginia Children’s Hospital, VA  Akron Children's Hospital, OH  Phoenix Childrens Hospital, Phoenix, AZ  University of Missouri School of Medicine, Columbia, MO  Rare Disease Research - NC, LLC, Hillsborough, NC  Capricor Therapeutics Inc, Cambridge, MA  Capricor Therapeutics Inc, NJ  capricor Therapeutics Inc, CA  

Reshaping Clinicians' Perceptions of Disease Burden in Becker Muscular Dystrophy: The Impacts of Incorporating the Patient Perspectives in CME

Author:Drexel, Carole   Wilson, Eve   Veerapandiyan, Aravindhan   Bello, Luca   Kowalski, Katie   

Session Name:P2: Education, Research, and Methodology: Neurohumanities and Education  

Topic:Education, Research, and Methodology  

Program Number:P2.005  

Author Institution:PlatformQ LLC, Needham, MA  PlatformQ LLC, Bowie, MD  Arkansas Childrens Hospital/UAMS, Little Rock, AR  University of Padova, Department of Neuroscience NPSRR, Padova, Italy  National Organization for Rare Disorders, Washington, DC