Browse All

Current Filters

CLEAR FILTER x

TITLE

A Prospective Longitudinal Observational Study in Myotonic Dystrophy Type One: From Clinical Outcomes to Trial Design

Author:Sansone, Valeria   Ferrari Aggradi, Carola   Lizio, Andrea   Nani, Michela   Dekdebrun, Jeanne   Eichinger, Katy   Gagnon, Cynthia   Subramony, S   Roxburgh, Richard   Hamel, Johanna   Statland, Jeffrey   Mul, Karlien   van Engelen, Baziel   Elsheikh, Bakri   Arnold, William   Turner, Chris   Schoser, Benedikt   Ragole, Thomas   Matthews, Emma   Sampson, Jacinda   Takahashi, Massanori   Wicklund, Matthew   Swenson, Andrea   Laverty, Chamindra   Shieh, Perry   Greene, Ericka   Hung, Man   Langeslay, Ruby   Raymond, Jennifer   Thornton, Charles   Johnson, Nicholas   

Session Name:P8: Neuromuscular and Clinical Neurophysiology (EMG): Muscle Disorders  

Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

Program Number:P8.003  

Author Institution:The NeMO Clinical Center - Neurorehabilitation Unit, University of Milan, Milan, Italy  University of Rochester, NY  University of Rochester, Rochester, NY  Sherbrooke University, QC, Canada  University of Florida, Gainesville, FL  Auckland Hospital, Auckland, New Zealand  University of Rochester, Neurology, Rochester, NY  University of Kansas Medical Center, Kansas City, KS  Radboud University, Nijmegen, Netherlands  Radboud University Nijmegen Medical Centre, Nijmegen, Netherlands  The Ohio State University Wexner Medical Center, Columbus, OH  University of Missouri, Columbus, OH  University College London, United Kingdom  Friedrich-Baur Institut, Munich, Germany  University of Colorado Department of Neurology, Aurora, CO  Atkinson-Morley Neuromuscular Centre, London, United Kingdom  Stanford University, PALO ALTO, CA  Clinical Neurophysiology, Osaka University, Suita, Japan  UT Health San Antonio, San Antonio, TX  University of Iowa Hospitals and Clinics, Iowa City, IA  UC San Diego, San Diego, CA  UCLA, Los Angeles, CA  Methodist Hospital, Houston, TX  Roseman University , UT  Virginia Commonwealth University, VA  University of Rochester Medical Center, Rochester, NY  Virginia Commonwealth University, Richmond, VA  

Design of Phase Three of KYSA-6, a Global Open-label, Randomized, Controlled Study of KYV-101, a Fully Human CD19 Chimeric Antigen Receptor (CAR) T-cell Therapy, Versus Ongoing Standard-of-Care (SOC) Immunosuppressive Therapy in Generalized Myasthenia Gr

Author:Mupiddi, Sri   Hunter, Michael C   Hoffmann, Sarah   Hegelmaier, Tobias   Motte, Jeremias   Gold, Ralf   Mougiakakos, Dimitrios   Schubert, Charlotte   Schreiber, Stefanie   Habib, Ali   Geis, Christian   Carbunar, Olimpia   Shroff, Sheetal   Dalakas, Marinos   Berthele, Achim   Shieh, Perry   Barboi, Alexandru   Dutra, Livia   Alsolaihim, Alanood   Needham, Edward   Norwood, Fiona   Cutter, Gary R   Hunter, Brad   Chou, Justin   Xing, Baodong   Borie, Dominic   Gehchan, Naji   Haghikia, Aiden   

Session Name:P9: Neuromuscular and Clinical Neurophysiology (EMG): Myasthenia Gravis Clinical Trials  

Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

Program Number:P9.011  

Author Institution:Stanford, CA  Intermountain Medical Center, UT  Charité-Universitätsmedizin Berlin, 10117 Berlin, Germany  Hannover Medical School, Germany  Ruhr University Bochum, Germany  Otto von Guericke University Magdeburg, Magdeburg, Germany  University Medical Center Hamburg-Eppendorf, Germany  Otto-von-Guericke University Magdeburg, Germany  University of California, Irvine, Orange, CA  Jena University Hospital, Germany  University of Miami, Miami, FL  Houston Methodist Hospital, Houston, TX  Thomas Jefferson University, Philadelphia, PA  School of Medicine, Technical University Munich, Klinikum rechts der Isar, Dept., Muenchen, Germany  University of California Los Angeles, Los Angeles, CA  Indiana University Health, IN  Instituto do Cérebro do Hospital Israelita Albert Einstein, Brazil  King Faisal Specialist Hospital and Research Center, Saudi Arabia  University of Cambridge, United Kingdom  Kings College Hospital, United Kingdom  University of Alabama , AL  Intermountain Health, UT  Kyverna Therapeutics Inc., CA  Kyverna Therapeutics Inc., Emeryville, CA  Hannover Medical School, Hannover, Germany