Development of a Clinical Tool to Aid in the Diagnosis of Duchenne Muscular Dystrophy

X-Linked Charcot-Marie-Tooth Disease in a 14-Year-Old Boy Presenting with Transient Neurological Symptoms and Leukoencephalopathy

A Phase 3, Open-Label, Single-Arm, Multicenter Study to Evaluate Ravulizumab Administered Intravenously in Pediatric Patients With Anti-Acetylcholine Receptor Antibody-Positive (AChR-Ab+) Generalized Myasthenia Gravis (gMG)