Browse All

Current Filters

CLEAR FILTER x

TITLE

Title
    Author Last Name
      Session Name
        Topic
          Program Number
            Author Institution

              Safety and Efficacy of DYNE-251 in Males with DMD Mutations Amenable to Exon 51 Skipping

              Author:Shieh, Perry   Campbell, Craig   Deconink, Nicolas   De Waele, Liesbeth   Flanigan, Kevin   Lorentzos, Michelle   Phan, Han   Mix, Chris   Ray, Soma   Wang, Dazhe   Dugar, Ashish   Kerr, Douglas   Naylor, Maria   Guglieri, Michela   

              Session Name:S31: Hot Topics in Child Neurology  

              Topic:Child Neurology and Developmental Neurology  

              Program Number:S31.010  

              Author Institution:University of California Los Angeles, Los Angeles, CA  London Health Sciences Centre, London, ON, Canada  Neuromuscular Reference Center UZ Gent, Gent, Belgium  University Hospitals Leuven, Leuven, Belgium  Nationwide CHildrens Hospital, Columbus, OH  Children's Hospital at Westmead, Westmead, New South Wales, Australia  Rare Disease Research, LLC, Atlanta, GA  Dyne Therapeutics, Inc., Waltham, MA  Royal Victoria Infirmary, Newcastle University, Newcastle-Upon-Tyne, United Kingdom