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              Effect Size Analysis of Cipaglucosidase Alfa Plus Miglustat Versus Alglucosidase Alfa in ERT-experienced Adults with Late-onset Pompe Disease in PROPEL

              Author:Kushlaf, Hani   Bratkovic, Drago   Byrne, Barry   Claeys, Kristl   Diaz-Manera, Jordi   Dimachkie, Mazen   Kishnani, Priya   Roberts, Mark   Toscano, Antonio   Castelli, Jeff   Holdbrook, Frederick   Das, Sheela   Wasfi, Yasmine   Schoser, Benedikt   Mozaffar, Tahseen   

              Session Name:S21: Inherited Myopathies and Neuropathies: New Therapeutic Approaches and Observations  

              Topic:Neuromuscular and Clinical Neurophysiology (EMG)  

              Program Number:S21.003  

              Author Institution:University of Cincinnati, Cincinnati, OH  PARC Research Clinic, Royal Adelaide Hospital, Adelaide, SA, Australia  University of Florida, Gainesville, FL  Department of Neurology, University Hospitals Leuven, and Laboratory for Muscle Diseases and Neuropathies, Department of Neurosciences, KU Leuven, Leuven, Belgium  John Walton Muscular Dystrophy Research Centre, Newcastle University, Newcastle, United Kingdom  Department of Neurology, University of Kansas Medical Center, Kansas City, KS  Duke University Medical Center, Durham, NC  Salford Royal NHS Foundation Trust, Salford, United Kingdom  ERN-NMD Center for Neuromuscular Disorders of Messina, Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy  Amicus Therapeutics, Inc., Princeton, NJ  Friedrich-Baur-Institute at the Department of Neurology, LMU University Hospital, LMU Munich, Munich, Germany  Department of Neurology, University of California, Irvine, CA  

              NEO1/NEO-EXT Studies: Long-term Muscle Quantitative Magnetic Resonance Imaging and Functional Efficacy in Adults With Late-onset Pompe Disease (LOPD) on Avalglucosidase Alfa Treatment

              Author:Ladha, Shafeeq   Carlier, Pierre   Vissing, John   Dimachkie, Mazen   Byrne, Barry   Barohn, Richard   Kishnani, Priya   Mengel, Eugen   Sacconi, Sabrina   Trivedi, Jaya   Young, Peter   an Haack, Kristina   Armstrong, Nicole   Miossec, Patrick   Thibault, Nathan   Sparks, Susan   Schoser, Benedikt   Diaz-Manera, Jordi   

              Session Name:P8: General Neurology: Assorted Neurologic Basic Science  

              Topic:General Neurology  

              Program Number:P8.010  

              Author Institution:Gregory W. Fulton ALS and Neuromuscular Center, Barrow Neurological Institute, Phoenix, AZ  Université Paris-Saclay, CEA, DRF, Service Hospitalier Frédéric Joliot, Orsay, France  Copenhagen Neuromuscular Center, Rigshospitalet, University of Copenhagen, Copenhagen, Denmark  University of Kansas Medical Center, Kansas City, KS  University of Florida, Gainesville, FL  University of Missouri, Columbia, MO  Duke University Medical Center, Durham, NC  SphinCS GmbH, Institute of Clinical Science for LSD, Hochheim, Germany  Neuromuscular Diseases Centre, University Hospital of Nice (CHU), Nice, France  University of Texas Southwestern Medical Center, Dallas, TX  Medical Park Bad Feilnbach, Bad Feilnbach, Germany  Sanofi, Chilly-Mazarin, France  Sanofi, Cambridge, MA  Friedrich-Baur-Institute, Ludwig-Maximilians-University Klinikum München, Munich, Germany  John Walton Muscular Dystrophy Research Centre, Newcastle University and Newcastle Hospitals NHS Foundation Trust, Newcastle, United Kingdom