Treatment Outcomes and Healthcare Resource Utilization Among People Living with Focal Onset Epilepsy and Deemed to be Drug Resistant in Clinical Practices in the United States
Jianbin Mao1, Koji Takahashi1, Mu Cheng2, Churong Xu2, Andra-Ecaterina Boca2, Ann Dandurand1, Yan Song2
1Cerevel Therapeutics, 2Analysis Group
Objective:
This study aims to understand the management and treatment outcomes of patients with drug-resistant focal onset seizures in the United States (US).  
Background:
In the US, about 3.4 million people are living with epilepsy. Approximately 20%-30% of people living with focal-onset seizures (FOS) are refractory to anti-seizure medications (ASMs). Drug-resistant (DR) epilepsy is defined by International League Against Epilepsy (ILAE) as failing 2 adequate trials of appropriate and tolerated ASMs.
Design/Methods:

Individual-level data were extracted from medical charts by neurologists/epileptologists at various clinical practices in the US. Eligible adult subjects had confirmed FOS and initiated 3rd line ASM therapy (LT) (indicating DR per ILAE definition, initiation date = index date), and had medical history available for ≥1 year before (baseline) and ≥2 years after index date (follow-up period). No minimum follow-up was required for subjects initiating cenobamate.

 

Results:

Study included 345 subjects. Mean (SD) age was 32.4 (11.2) years, 65.5% male, 78.3% White/Caucasian, and 64.6% covered by commercial/private insurance. The most prevalent baseline neuropsychiatric comorbidities were anxiety (31.6%), depression (29.3%) and migraine (13.3%). The frequent baseline ASM regimens were all monotherapies:  levetiracetam (25.2%), carbamazepine (13.3%) and phenytoin/fosphenytoin (12.5%) in 1st LT; levetiracetam (11.3%), lamotrigine (8.4%) and carbamazepine (5.8%) in 2nd LT. All subjects had ≥1 seizure/month during the last 6 months of baseline: mean (SD) rate 6.1 (7.7) seizures/month. At follow-up, the mean (SD) was 3.8 (7.2) seizures/month. Compared to baseline, 27%, 22%, 18%, 5% and 28% subjects at follow-up experienced no (≤0%), some (1%-49%), moderate (50%-74%), significant (75-89%) and greatest (≥90%) seizure frequency reduction, respectively. At follow-up, 70% of hospitalizations were unplanned. Breakthrough seizures were the most common reason for hospitalization.  

Conclusions:

People with DR-FOS have significant comorbidities. Most do not have sufficient seizure control after initiating 3rd LT treatment and utilize significant healthcare resources. 

10.1212/WNL.0000000000204344